Facetten
Zugriff
Einrichtung
Medientyp
- Text 4
Karte
Erscheinungsjahr
Autor/in
- Jacoby, David
- Slasor, Peter 4
- Ajayi, Temitayo 3
- Schulz, Angela 3
- Kohlschütter, Alfried 2
- alle zeigen
Sprache
- Englisch 4
4 Einträge gefunden
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Clinical Pharmacokinetics and Pharmacodynamics of Cerliponase Alfa, Enzyme Replacement Therapy for CLN2 Disease by Intracerebroventricular Administration
2021 - Forschungsinformationssystem des UKE - frei zugänglich -
Study of Intraventricular Cerliponase Alfa for CLN2 Disease
- Schulz, Angela
- Ajayi, Temitayo
- Specchio, Nicola
- de Los Reyes, Emily
- Gissen, Paul
- Ballon, Douglas
- Dyke, Jonathan P
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An Adapted Clinical Measurement Tool for the Key Symptoms of CLN2 Disease
- Wyrwich, K W
- Schulz, Angela
- Nickel, Miriam
- Slasor, Peter
- Ajayi, Temitayo
- Jacoby, David
- Kohlschütter, Alfried
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Disease characteristics and progression in patients with late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease: an observational cohort study
- Nickel, Miriam
- Simonati, Alessandro
- Jacoby, David
- Lezius, Susanne
- Kilian, Dirk
- Van de Graaf, Benjamin
- Pagovich, Odelya E