Facetten
Zugriff
Einrichtung
Medientyp
- Text 4
Karte
Erscheinungsjahr
Autor/in
- Wijburg, Frits A
- Barić, Ivo 3
- Burlina, Alberto B 3
- Valayannopoulos, Vassili 3
- Dionisi-Vici, Carlo 2
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Sprache
- Englisch 4
4 Einträge gefunden
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A multicenter open-label extension study of intrathecal heparan-N-sulfatase in patients with Sanfilippo syndrome type A
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Impact of age at onset and newborn screening on outcome in organic acidurias
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