Facetten
Zugriff
Einrichtung
Medientyp
- Text 2
Karte
Erscheinungsjahr
- 2021 2
Autor/in
- Gissen, Paul
- Schwering, Christoph
- Specchio, Nicola 2
- Butt, Thomas 1
- Camp, Charlotte 1
- alle zeigen
Sprache
- Englisch 2
2 Einträge gefunden
-
Cerliponase Alfa for the Treatment of Atypical Phenotypes of CLN2 Disease:A Retrospective Case Series
- Wibbeler, Eva
- Wang, Raymond
- Reyes, Emily de Los
- Specchio, Nicola
- Gissen, Paul
- Guelbert, Norberto
- Nickel, Miriam
-
Investigating health-related quality of life in rare diseases:a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2)
- Gissen, Paul
- Specchio, Nicola
- Olaye, Andrew
- Jain, Mohit
- Butt, Thomas
- Ghosh, Wrik
- Ruban-Fell, Benjamin