Facetten
Zugriff
Einrichtung
Medientyp
- Text 4
Karte
Erscheinungsjahr
Autor/in
- Specchio, Nicola
- Gissen, Paul 3
- Ajayi, Temitayo 2
- Jacoby, David 2
- Schulz, Angela 2
- alle zeigen
Sprache
- Englisch 4
4 Einträge gefunden
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Investigating health-related quality of life in rare diseases:a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2)
- Gissen, Paul
- Specchio, Nicola
- Olaye, Andrew
- Jain, Mohit
- Butt, Thomas
- Ghosh, Wrik
- Ruban-Fell, Benjamin
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Clinical Pharmacokinetics and Pharmacodynamics of Cerliponase Alfa, Enzyme Replacement Therapy for CLN2 Disease by Intracerebroventricular Administration
2021 - Forschungsinformationssystem des UKE - frei zugänglich -
Cerliponase Alfa for the Treatment of Atypical Phenotypes of CLN2 Disease:A Retrospective Case Series
- Wibbeler, Eva
- Wang, Raymond
- Reyes, Emily de Los
- Specchio, Nicola
- Gissen, Paul
- Guelbert, Norberto
- Nickel, Miriam
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Study of Intraventricular Cerliponase Alfa for CLN2 Disease
- Schulz, Angela
- Ajayi, Temitayo
- Specchio, Nicola
- de Los Reyes, Emily
- Gissen, Paul
- Ballon, Douglas
- Dyke, Jonathan P