Facetten
Zugriff
Einrichtung
Medientyp
- Text 4
Karte
Erscheinungsjahr
Autor/in
- Cleary, Maureen
- Burlina, Alberto 3
- Muntau, Ania C 3
- Blau, Nenad 2
- Bélanger-Quintana, Amaya 2
- alle zeigen
Sprache
- Englisch 4
4 Einträge gefunden
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Long-term efficacy and safety of sapropterin in patients who initiated sapropterin at < 4 years of age with phenylketonuria: results of the 3-year extension of the SPARK open-label, multicentre, randomised phase IIIb trial
- Muntau, Ania C
- Burlina, Alberto
- Eyskens, François
- Freisinger, Peter
- Leuzzi, Vincenzo
- Sivri, Hatice Serap
- Gramer, Gwendolyn
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A multicenter open-label extension study of intrathecal heparan-N-sulfatase in patients with Sanfilippo syndrome type A
- Wijburg, Frits A
- Whitley, Chester B
- Muenzer, Joseph
- Gasperini, Serena
- Del Toro, Mireia
- Muschol, Nicole
- Cleary, Maureen
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Diagnostic and management practices for phenylketonuria in 19 countries of the South and Eastern European Region: survey results: survey results
- Giżewska, Maria
- MacDonald, Anita
- Bélanger-Quintana, Amaya
- Burlina, Alberto
- Cleary, Maureen
- Coşkun, Turgay
- Feillet, François
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