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Medientyp
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- Denecke, Jonas
- Johannsen, Jessika 2
- Wiegand-Grefe, Silke 2
- Barkmann, Claus 1
- Becker, Lena-Luise 1
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3 Einträge gefunden
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Health-Related Quality of Life and mental health of families with children and adolescents affected by rare diseases and high disease burden: the perspective of affected children and their siblings
- Wiegand-Grefe, Silke
- Liedtke, Anna
- Morgenstern, Lydia
- Hoff, Antonia
- Csengoe-Norris, Anikó
- Johannsen, Jessika
- Denecke, Jonas
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Gene replacement therapy with onasemnogene abeparvovec in children with spinal muscular atrophy aged 24 months or younger and bodyweight up to 15 kg: an observational cohort study
- Weiß, Claudia
- Ziegler, Andreas
- Becker, Lena-Luise
- Johannsen, Jessika
- Brennenstuhl, Heiko
- Schreiber, Gudrun
- Flotats-Bastardas, Marina