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Zugriff
Einrichtung
Medientyp
- Text 2
Karte
Erscheinungsjahr
Autor/in
- Burlina, Alberto 2
- Eyskens, François 2
- Freisinger, Peter 2
- Gramer, Gwendolyn 2
- Leuzzi, Vincenzo
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Sprache
- Englisch 2
2 Einträge gefunden
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Long-term efficacy and safety of sapropterin in patients who initiated sapropterin at < 4 years of age with phenylketonuria: results of the 3-year extension of the SPARK open-label, multicentre, randomised phase IIIb trial
- Muntau, Ania C
- Burlina, Alberto
- Eyskens, François
- Freisinger, Peter
- Leuzzi, Vincenzo
- Sivri, Hatice Serap
- Gramer, Gwendolyn
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Efficacy, safety and population pharmacokinetics of sapropterin in PKU patients <4 years: results from the SPARK open-label, multicentre, randomized phase IIIb trial
- Muntau, Ania C
- Burlina, Alberto
- Eyskens, François
- Freisinger, Peter
- De Laet, Corinne
- Leuzzi, Vincenzo
- Rutsch, Frank